12 février 2024
ELSIBI
Hypothèses : carnets de recherches en Sciences humaines et sociales
OpenEdition
info:eu-repo/semantics/openAccess
lsgilbert, « MHRA authorises world-first gene therapy that aims to cure sickle-cell disease and transfusion-dependent β-thalassemia », ELSIBI, ID : 10.58079/vto2
Casgevy (exagamglogene autotemcel) is based on the innovative gene-editing tool CRISPR, which won its inventors the Nobel Prize in 2020. Read the press release from Medicines and Healthcare products Regulatory Agency published on 16 November 2023.